HD Patients Prefer Less Invasive, No-Placebo Gene Therapy Trials, Survey Says

HD Patients Prefer Less Invasive, No-Placebo Gene Therapy Trials, Survey Says

Publication date: Aug 08, 2019

This post was originally published on this site Eligible Huntington’s disease patients would likely participate in a gene therapy trial regardless of the study design, but they are more inclined toward those with less invasive interventions and without a placebo group, a questionnaire-based study suggests. The results may be useful to design more patient-centered clinical trials assessing the effects of gene therapy in Huntington’s patients. With the development of new gene or molecular therapies to halt or prevent the development of Huntington’s disease – mainly administered through more invasive procedures – it is important to understand patients’ concerns and willingness to participate in these trials. Researchers at Penn designed a questionnaire to evaluate how patient clinical status, study design, and therapy goals can influence the willingness of eligible Huntington’s patients to participate in gene therapy trials. The post HD Patients Prefer Less Invasive, No-Placebo Gene Therapy Trials, Survey Says appeared first on Huntington’s Disease News.

Concepts Keywords
Brain Management of depression
Clinical Trial Placebo-controlled study
Clinical Trials Therapy
Demographic Patient recruitment
Genetic Placebo
Genetic Counselor Drug discovery
Huntington Design of experiments
Interest Group Clinical trials
Multiple Choice Pharmaceutical industry
Mutation Clinical research
Neurology Articles
Patient Participation Health
Pennsylvania Molecular therapies
Placebo Experimental therapy
Questionnaire Invasive procedures
Spinal Cord Huntington s disease
Survey

Semantics

Type Source Name
gene UNIPROT IMPACT
pathway BSID Release
drug DRUGBANK Tropicamide
disease MESH development
gene UNIPROT FANCE
gene UNIPROT ELOVL6
disease DOID face
gene UNIPROT SLC35G1
gene UNIPROT DESI1

Similar

Original Article

Leave a Comment

Your email address will not be published. Required fields are marked *